The first gene therapy for a deadly form of muscular dystrophy received preliminary U.S. approval on Thursday despite concerns from some government scientists about the treatment's ability to help ...

The first gene therapy for children with Duchenne muscular dystrophy has been approved by the U.S. Food and Drug Administration. The therapy can be used in 4- and 5-year-olds with the degenerative ...

The drug, from biotech company Sarepta Therapeutics, will need to prove in an ongoing clinical trial that it improves physical function and mobility in patients with Duchenne muscular dystrophy in ...

JENKS, Okla. — A local gym is raising money to send kids with muscular dystrophy to a summer camp specialized for them. Burn Boot Camps everywhere are fundraising for the Muscular Dystrophy ...

COLORADO SPRINGS, Colo. (KRDO) -- A groundbreaking gene therapy was recently approved by the U.S. Food and Drug Administration to treat the most common form of muscular dystrophy in children, Duchenne ...

Becker muscular dystrophy (BMD) is a type of muscular dystrophy, a genetic condition that weakens and damages muscles. It can worsen with age. However, its symptoms are less severe than those of ...

July 26 (UPI) --A new test could speed the diagnosis of spinal muscular atrophy, a rare but deadly progressive muscle-wasting disorder, in infants. And a new way to screen for urinary tract infections ...

(CNN) — The US Food and Drug Administration has approved the first gene therapy to treat a rare and devastating muscle disease but limited the approval to kids ages 4 and 5 based on available evidence ...